UPDATE ON EXON SKIPPING

Dear all,

Today Judith van Deutekom, Prosensa and LUMC Leiden, will present on the World Muscle Society conference in Brugge the preliminary results of the ongoing clinical trial in the Netherlands.

After intra muscular injection of AON skipping exon 51 in the first patiënt, they were able to demonstrate the presence of truncated Dystrophin in the biopsy which was taken earlier this week, one month after injection. So far 3 patients are injected without side effects.

Although more results will follow in the next month we felt you all might like to know this first information.

Kind regards,

Elizabeth Vroom       
Amsterdam, October 2006
UPPMD

and

Pat Furlong, President
Parent Project Muscular Dystrophy

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